Patisiran (Onpattro®) – Treats polyneuropathy

Patisiran is the first-ever RNA interference drug consisting of short, double-stranded interfering ribonucleic acid (siRNA) encapsulated in a lipid nanoparticle and targeted to inhibit hepatic synthesis of transthyretin, both the wild-type and mutant. [source: Pubmed]

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Patisiran (Onpattro®) – Treats polyneuropathy

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