Prednisone (steroid)
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treatments
Tafamidis Meglumine (Vyndaqel®) Treats Cardiomyopathy
Both Vyndaqel and Vyndamax contain the same active ingredient called tafamidis. The difference between Vyndaqel and Vyndamax lies in the form of tafamidis they contain. Vyndaqel contains the micronized meglumine salt of tafamidis, while Vyndamax contains the free acid form of tafamidis
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Inotersen (Tegsedi®) – Treats polyneuropathy
TEGSEDI is the first and only self-administered injection for the polyneuropathy of hATTR amyloidosis in adults. Regular lab monitoring of platelet count and renal liver function is required during treatment with TEGSEDI.
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Bone Marrow / Stem Cell Transplant
Stem cell transplantation (SCT) is an effective treatment for amyloidosis , but it’s not a cure. Amyloidosis will return in everyone. However, some patients have been successfully treated with SCT and have been able to receive another SCT when their disease progressed.
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Patisiran (Onpattro®) – Treats polyneuropathy
Patisiran is the first-ever RNA interference drug consisting of short, double-stranded interfering ribonucleic acid (siRNA) encapsulated in a lipid nanoparticle and targeted to inhibit hepatic synthesis of transthyretin, both the wild-type and mutant. [source: Pubmed]
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